Girl with genetic deafness regains hearing after gene therapy in one ear

An 18-month-old girl born deaf due to an OTOF gene mutation can now hear sounds and has begun speaking. She received an experimental gene therapy infusion in her right ear at 11 months old as part of a Cambridge University trial. This is a single patient result from an early-stage trial, and the outcome has not yet been peer-reviewed, being based on clinician and family accounts. The long-term durability of the effect is not yet known.

CHECKED · 1 SOURCE · UNCORROBORATED ✓